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Innovative Designs and Analyses for Small Population Clinical Trials

Development Strategies and Operational Engagement for Pediatric and Rare Diseases

Jezik AngleščinaAngleščina
E-knjiga Adobe ePub DRM
Založba Springer, november 2024
This book discusses a multidisciplinary and multi-stakeholder collaborative approach to small popula... Celoten opis
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This book discusses a multidisciplinary and multi-stakeholder collaborative approach to small population clinical trials. It provides and illustrates a systematic framework that depends upon a collaborative infrastructure between the patient community, patient advocacy groups, researchers and investigators, pharmaceutical companies, global regulatory agencies, and customers. The book also highlights the considerations of natural history and patient registry, diagnostic criteria determination, identification of clinically meaningful endpoints, and global regulatory guidance. The authors detail the nuances of clinical trial design as specific to small population disease, drawing from real examples.

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Polni naslov Innovative Designs and Analyses for Small Population Clinical Trials
Jezik Angleščina
Vezava E-knjiga - Adobe ePub DRM
Datum izida 2024
EAN 9783031608438
Koda Libristo 47697533
Založba Springer
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